The last couple of weeks has been particularly distressing for Duchenne muscular dystrophy patients and their families. The ...

The agency’s now-reversed decision to halt distribution of a gene therapy for children suffering from muscular dystrophy ...

The Food and Drug Administration has paused distribution of the gene therapy Elevidys following the death of a third patient ...

Vinay Prasad has stepped down as head of the FDA’s biologics division just two months into the job, following growing ...

European Medicines Agency recognizes potential of lead compound MP1032 in addressing a high unmet medical need in Duchenne Muscular Dystrophy (DMD)Designation is paving the way for safer long-term ...

The FDA said it was clearing the way for Sarepta Therapeutics to resume shipments of its gene therapy for Duchenne muscular ...

Genethon is determined to bring GNT0004 to market for young patients and their families who are waiting for a therapeutic ...

Duchenne, one of the most severe forms of muscular dystrophy, affects about one out of every 3,600 boys. The inherited rare disease on the X chromosome is caused by a genetic defect and it ...

On Thursday 28 August, Sam Taylor, 46, his wife Sue, 47, and daughter Beth, 17, from Crooklands in Cumbria will set off to ...

Duchenne Muscular Dystrophy Treatment Drugs, Clinical Trials, Pipeline Insights and Companies 2024 GetNews - TGAM - GetNews - Wed Sep 25, 2024 ...

LONDON, ON, May 19, 2025 /CNW/ - On May 25, Canadians are walking, running, and rolling in support of the 30th annual Walk to Defeat Duchenne, the country's only national event dedicated to ...

The fact the study shines light on how Duchenne muscular dystrophy might operate offers sufferers and their families a degree of hope, said Debra Chiabai, whose 15-year-old son Alex has the disorder.