All patients in the first cohort achieved between 27- to 208-fold increases in α-Gal A activity relative to mean normal level ~ ~ Preliminary data show AMT-191 has a manageable safety profile at the ...

JCR Pharmaceuticals Co., Ltd. (TSE 4552; “JCR”), a global biopharmaceutical company dedicated to developing therapies for rare and genetic diseases, presented new data from its pipeline of ...

MAIA Biotechnology, Inc. (NYSE American: MAIA) ("MAIA”, the "Company”), a clinical-stage biopharmaceutical company focused on developing targeted immunotherapies for cancer, today announced that an ...

Travere Therapeutics, Inc., (Nasdaq: TVTX) today announced that the Company shared two oral presentations in classical homocystinuria (HCU) at the International Congress of Inborn Errors of Metabolism ...

Loss of Polβ leads to increased mutations in developing neurons, potentially contributing to neurodevelopmental disorders.A ...

Mayo Clinic researchers have pinpointed how excessive alcohol consumption contributes to fatty liver disease, a condition ...

BRAIN Biotech AG, a leading provider of integrated solutions for the biologization of industry, has appointed Johan Jansen-Storbacka as Executive Vice President of the BRAINBiocatalysts' ...