Gene therapy Gene therapy works by directly altering a person’s genes in order to treat a disease or condition. There are a few different ways of doing this. Previous studies that have used gene ...

We spoke with the developers and manufacturers of the CRISPR gene therapy used to treat KJ Muldoon’s rare genetic condition, CPS1, about how the product was created in just six months.

The immune system is trained to destroy viruses, even when they carry therapeutic cargo as is the case in gene therapy. Now researchers have figured out how to dial down the immune response.

French scientists mixed gene therapy and bone marrow transplants in two boys to seemingly halt the fatal brain disease best known from the movie "Lorenzo's Oil." ...

Bar-Ilan University scientist part of €8 million consortium to ensure accuracy in CAR-T cell therapy, an immunotherapy using ...

For years, Stephanie McCabe and Andre Doucette accepted that their six-year-old son Emmett would die young. Now a possible treatment for Sanfilippo syndrome is changing everything for the Saskatoon ...

Drug developer Suma Krishnan was 51 when she had the idea for a topical gene therapy to treat a rare and terrible skin disorder, called dystrophic epidermolysis bullosa, in which the skin becomes ...

Cellworks Group Inc., a leader in Personalized Therapy Decision Support and Best-in-Class PTRS, today announced results from a new study showing that the combination of tumor microenvironment (TME) ...