Today, gene-editing drug developers most typically spend a lot of time assembling bespoke analytical workflows to characterize any off-target edits made by their therapy and demonstrate safety.

For the first time, doctors have created a customized treatment using the revolutionary gene-editing technique known as CRISPR to treat a baby with a rare, life-threatening genetic disorder.

The do-it-yourself (DIY) biohack movement is here, and it’s turning science into a communal experiment. High schoolers in Seattle have engineered bacteria in science fairs, while biohackers like ...

A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing treatment made just for him.

A team of doctors at the Children's Hospital of Philadelphia and Penn Medicine treated a baby with a gene editing technology customized for his rare disease for the first time ever.

Baby saved by gene-editing therapy 'graduates' from hospital, goes home KJ Muldoon was diagnosed with a rare, deadly genetic disease after he was born.